6MWT	6 min walking test
ABC	approximate Bayesian computation model
AE	adverse event
CI	confidence interval
OPD	infantile-onset Pompe disease
ERT	enzyme replacement therapy
FVC	forced vital capacity
GAA	acid alpha-glucosidase
GLMM	generalized linear mixed model
IAR	infusion-associated reaction
IgG	immunoglobulin G
IR	incidence rate
LOPD	late-onset Pompe disease
LOTS	late-onset treatment study
ML	maximum likelihood
MRC	Medical Research Council
NB	newborn
NRSI	non-randomized studies of interventions
PD	Pompe disease
PedsQL	Pediatric Quality of Life Inventory™
PICO	patients, intervention, control, outcome
QOL	quality of life
RCT	randomized clinical trial
REML	restricted maximum-likelihood estimator
RoB	Risk of Bias tool
ROBINS-I	Risk Of Bias In Non-randomized Studies of Interventions tool
SM	Supplementary Materials
TOV	time on ventilatory support
WGMS	Walton and Gardner-Medwin Scale