Official websites use .gov
A
.gov website belongs to an official
government organization in the United States.
Secure .gov websites use HTTPS
A lock (
) or https:// means you've safely
connected to the .gov website. Share sensitive
information only on official, secure websites.
Cohort of 7 SMA patients receiving onasemnogene abeparvovec early in life
Longitudinal plots for pNf-H concentrations, Nf-L concentrations, and CMAP values for each individual case (A–G) in this cohort. Arrows indicate the onasemnogene abeparvovec injection time point for each case.
