Official websites use .gov
A
.gov website belongs to an official
government organization in the United States.
Secure .gov websites use HTTPS
A lock (
) or https:// means you've safely
connected to the .gov website. Share sensitive
information only on official, secure websites.
Cohort of 6 SMA patients receiving co-therapy with nusinersen and onasemnogene abeparvovec early in life
Longitudinal plots for pNf-H concentrations, Nf-L concentrations, and CMAP values for each individual case (A–F) in this cohort. Red arrows indicate the first nusinersen dose and dark arrows indicate the onasemnogene abeparvovec injection. ∗Subject 913 received only a single loading dose of nusinersen (please see materials and methods for details).
