Table 1.
Structure, mechanism of action and side effects of NMD pathway inhibitors
Molecule | Structure | Mechanism of action | Side effects |
---|---|---|---|
Aminoglycosides [71] |
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PTC readthrough | Toxic at clinical active concentrations |
Caffeine [72] |
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SMG1 inhibition | Toxicity, highly aspecific by targeting several kinases |
NMDI-1 [73, 74] |
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Stabilization of the phosphorylated form of UPF1 | No side effects in mice |
5-azacytidine [75] |
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Non identified, but c-MYC-mediated | Already approved for the treatment of diverse malignancies |
Amlexanox [76] |
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Inhibits NMD at a late stage | Clinically approved for aphthous ulcers |
NMDI14 [77] |
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Disrupts the SMG7–UPF1 complex | Negligible toxicity in cell-based assays |