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. 2021 Nov 24;12:754073. doi: 10.3389/fphar.2021.754073

TABLE 1.

Federal list of high-cost diseases, including rare diseases.

No High-cost diseases, including rare diseases Code a
1 Hemophilia D66, D67, D68.0
2 Cystic fibrosis E84
3 Growth Hormone Deficiency E23.0
4 Gaucher disease E75.2
5 Tumors of the hematopoietic and lymphoid tissues C92.1, C88.0, C90.0, C82, C83.0, C83.1, C83.3, C83.4, C83.8, C83.9, C85, C91.1
6 Multiple Sclerosis G35
7 Hemolytic-uremic syndrome D59.3
8 Systemic-onset juvenile rheumatoid arthritis M08.2
9 Mucopolysaccharidosis type I E76.0
10 Mucopolysaccharidosis type II E76.1
11 Mucopolysaccharidosis type IV E76.2
12 Unspecified aplastic anemia D61.9
13 Inherited factor II deficiency (fibrinogen), factor VII deficiency (labile), factor X deficiency (Stewart-Prauer) D68.2
14 Patients after organ and/or tissue transplantation Z94.0, Z94.1, Z94.4, Z94.8
a

International Statistical Classification of Diseases and Related Health Problems, 10th revision.