Table 1.
Characteristic | Untreated groupa (N = 30) |
Age, y | |
Mean±SD | 8.8±1.8 |
Min, max | 7.0, 13.0 |
Weight, kg | |
Mean (SD) | 30.6±9.9 |
Min, max | 17.9, 53.2 |
Standing height, cm | |
Mean (SD) | 122.8±9.0 |
Min, max | 108.0, 142.5 |
Time since DMD diagnosis at baseline, mo | |
Mean (SD) | 54.7±31.6 |
Min, max | 12.7, 114.9 |
Corticosteroid treatment, n (%) | |
Deflazacort | 21 (70.0) |
Prednisone | 9 (30.0) |
Corticosteroid schedule, n (%) | |
Continuous | 24 (80.0) |
Intermittent | 2 (20.0) |
Abbreviations: DMD = Duchenne Muscular Dystrophy; SD =standard deviation. aIncluded patients with the following mutations: exon 12–44 (n = 1); exon 42–45 (n = 1); exon 43 (n = 1); exon 44 (n = 1); exon 45 (n = 2); exon 45–52 (n = 4); exon 46–47 (n = 3); exon 46–48 (n = 5); exon 46–50 (n = 1); exon 48–52 (n = 2); exon 49–52 (n = 2); exon 51 (n = 2); exon 51–53 (n = 2); exon 51–55 (n = 3).