Table 4.
Role of HSCT | Immune deficiency |
---|---|
Curative | SCID, CID, CGD, DOCK8, DOCK2, IPEX, WAS, WIP, ARPC1B, CD40L, XLP1, XLP2, APDS, MHC class II, AD HIGE, CTLA4 haploinsufficiency, LRBA, HLH 1–5, GATA2, RAB27A, LAD1, RD |
Partially curative | CHH, PGM3, STAT-1 and STAT-3 GOF, SCN, ADA2, C1Q, CD25, IL-10 & IL-10R deficiency, dsDNA break repair disorders |
Controversial | CVID, Agammaglobulinemia, other complement deficiencies, DGS, IKBA deficiency, NEMO |