Flowchart diagram outlining the primary methodologies used for
conducting the exome-by-phenome-wide association study and for evaluation of the
robustness of the associations, indicating that 97 genes had associations at a
significance level of p<E-06 via logistic regression. The pathways
starting with short descending arrows represent the 'discovery phase', in which
predicted loss-of-function (pLOF)-based gene burdens were studied on an
exome-by-phenome-wide scale in 10,900 individuals from the Penn Medicine Biobank
(PMBB). “Replication studies in PMBB” refers to analyses of
gene-phenotype associations using REVEL-informed missense-based gene burdens and
univariate analyses within the discovery PMBB cohort, as well as in an
independent cohort of African Americans in the PMBB (the PMBB2 cohort; N=6,432).
Additional replication studies included analyses of gene-phenotype associations
using pLOF-based gene burdens, REVEL-informed missense-based gene burdens, and
univariate analyses in BioMe (N=23,989), DiscovEHR (N=85,450), and the UK
Biobank (N=32,268), as well as univariate analyses in BioVU (N=66,400).