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Adverse Events Overview
| |
Part 1 |
Combined Parts 1 and 2 |
|
|---|---|---|---|
| AEs, n (%) | Placebo (n = 4) | Golodirsen (n = 8) | Total golodirsen (n = 25) |
| Patients with ≥1 AE, n (%) | 4 (100) | 8 (100) | 25 (100) |
| Related to study drug | 2 (50.0) | 5 (62.5) | 9 (36.0) |
| Serious | 0 | 0 | 4 (16.0) |
| Leading to study drug discontinuation | 0 | 0 | 0 |
| Total AEs by severity, n | 23 | 69 | 860 |
| Mild | 22 | 68 | 831 |
| Moderate | 1 | 1 | 24 |
| Severe | 0 | 0 | 5 |
AE, adverse event.
