AAV |
Adeno-associated virus |
AAVrh74.tMCK.hCAPN3 |
AAV rhesus 74 truncated muscle creatine kinase human CAPN3 |
AMBMP |
2-amino-4-(3,4-(methylenedioxy)benzylamino)-6-(3-methoxyphenyl) pyrimidine |
ATF6 |
Activating transcription factor 6 |
C3KO |
Calpain 3 knock out |
CaMKII |
Ca2+/calmodulin-dependent protein kinase II |
CaMKII |
Ca2+/calmodulin (CaM)-dependent protein kinase II |
CAPN3 |
Calpain 3 |
Cas9 |
Native Cas9 nuclease |
CHOP |
C/-EBP homologous protein |
CRISPR-Cas9 |
Clustered regularly interspaced short palindromic repeats CRISPR-associated proteins 9 |
CSQ |
Calsequestrin |
DMD |
Duchenne muscular dystrophy |
elF2α |
Eukaryotic initiation factor 2α |
ER |
Endoplasmic reticulum |
ERAD |
ER-associated protein degradation |
FRZB |
Frizzled-related protein |
GRP78 |
Glucose-regulated protein |
IPSC |
Induced pluripotent stem cell |
IRE1α |
Inositol-requiring enzyme 1α |
LGMDR1 |
Limb girdle muscular dystrophy R1 |
LIM |
Lin-11 Isl-1 Mec-3 |
Mss51 |
Mitochondrial translational activator |
MuRF1 |
Muscle RING-finger protein-1 |
MYO-029 |
Stamulumab |
MyoD |
Myogenic differentiation antigen |
NCX3 |
Na+-Ca2+ exchanger 3 |
pAAV-CMV-mSeAPpropmyoD76A |
Plasmid AAV-cytomegalovirus- murine-secreted alkaline phosphatase myogenic differentiation antigen murine-secreted alkaline phosphatase |
Pax3/Pax7 |
Paired box gene 3/Paired box gene 7 |
PERK |
PKR-like ER kinase |
RyR1 |
Ryanodine receptor 1 |
SERCA |
Sarcoplasmic/endoplasmic reticulum Ca2+ ATPase |
TCF/LEF |
T-cell factor/lymphoid enhancer factor |
TRIM32 |
Tripartite motif-containing protein 32 |
TUDCA |
Tauroursodeoxycholic acid |
UPR |
Unfolded protein response |
WNT |
Wingless-related integration site |
XBP1 |
X-box binding protein 1 |