| AAV | Adeno-associated virus |
| AAVrh74.tMCK.hCAPN3 | AAV rhesus 74 truncated muscle creatine kinase human CAPN3 |
| AMBMP | 2-amino-4-(3,4-(methylenedioxy)benzylamino)-6-(3-methoxyphenyl) pyrimidine |
| ATF6 | Activating transcription factor 6 |
| C3KO | Calpain 3 knock out |
| CaMKII | Ca2+/calmodulin-dependent protein kinase II |
| CaMKII | Ca2+/calmodulin (CaM)-dependent protein kinase II |
| CAPN3 | Calpain 3 |
| Cas9 | Native Cas9 nuclease |
| CHOP | C/-EBP homologous protein |
| CRISPR-Cas9 | Clustered regularly interspaced short palindromic repeats CRISPR-associated proteins 9 |
| CSQ | Calsequestrin |
| DMD | Duchenne muscular dystrophy |
| elF2α | Eukaryotic initiation factor 2α |
| ER | Endoplasmic reticulum |
| ERAD | ER-associated protein degradation |
| FRZB | Frizzled-related protein |
| GRP78 | Glucose-regulated protein |
| IPSC | Induced pluripotent stem cell |
| IRE1α | Inositol-requiring enzyme 1α |
| LGMDR1 | Limb girdle muscular dystrophy R1 |
| LIM | Lin-11 Isl-1 Mec-3 |
| Mss51 | Mitochondrial translational activator |
| MuRF1 | Muscle RING-finger protein-1 |
| MYO-029 | Stamulumab |
| MyoD | Myogenic differentiation antigen |
| NCX3 | Na+-Ca2+ exchanger 3 |
| pAAV-CMV-mSeAPpropmyoD76A | Plasmid AAV-cytomegalovirus- murine-secreted alkaline phosphatase myogenic differentiation antigen murine-secreted alkaline phosphatase |
| Pax3/Pax7 | Paired box gene 3/Paired box gene 7 |
| PERK | PKR-like ER kinase |
| RyR1 | Ryanodine receptor 1 |
| SERCA | Sarcoplasmic/endoplasmic reticulum Ca2+ ATPase |
| TCF/LEF | T-cell factor/lymphoid enhancer factor |
| TRIM32 | Tripartite motif-containing protein 32 |
| TUDCA | Tauroursodeoxycholic acid |
| UPR | Unfolded protein response |
| WNT | Wingless-related integration site |
| XBP1 | X-box binding protein 1 |