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Oligonucleotides other than ASOs and siRNAs in clinical development.
| Drug Name | Target Gene | Mode of Action (Type of Compound) |
Therapy Area | Latest Stage of Development | Company |
|---|---|---|---|---|---|
| Lademirsen | MIR21 | Expression inhibition (miRNA inhibitor) | Genitourinary system | Phase II | Sanofi |
| MTL-CEBPA | CEBPA | Expression activation (saRNA) | Oncology | Phase II | Mina Therapeutics |
| remlarsen | MIR29B1 | Expression activation (miRNA mimic) | Dermatology | Phase II | Miragen Therapeutics |
