Table 1.
Age (yrs) | |
---|---|
Mean (SD) | 9.1 (4.0) |
Range | 4 - 17 |
Gender, no. (%) | |
Male | 9 (64%) |
Female | 5 (36%) |
Race, no. (%) | |
White | 11 (79%) |
Black | 3 (21%) |
Laterality, no. (%) | |
Right Eye | 13 (48%) |
Left Eye | 14 (52%) |
RPE65 Variants, no. (%) | |
c.11+5G>A homozygous | 8 (57%) |
c.11+5G>A and c.962dupA, p.Asn321Lysfs | 2 (14%) |
c.11+5G>A and c.1249G>C, p.Glu417Gln | 1 (7%) |
c.74C>T, p.Pro25Leu and c.893delA, p.298Lysfs | 1 (7%) |
c.118G>A, p.Glu40Lys and c.1102T>C, p.Tyr368His | 1 (7%) |
c.271C>T, p.Arg91Trp and c.1334A>G, p.Asp445Gly | 1 (7%) |