Table 1. Impurity Considerations during Scale-up of the TT Modification and Conjugation Steps in the Absence of Oligosaccharide 2 and TT.
impurity | guideline for GMP | maximum allowed quantity in the formulated vaccine (μg/dose or μg/0.5 mL unless indicated otherwise) | maximum allowed quantity in the bulk vaccinea (mM) | estimated maximum concentration in the bulk vaccine (mM) |
---|---|---|---|---|
GMBS/GMBA | ICH-M7 | 12 | <9 | 15.2b |
N-hydroxysuccinimide | ICH-M7 | 12 | <9 | 15.2b |
DMSO | ICH-Q3D | 5000 ppm | <6400c | 761d |
hydroxylamine·HCl | ICH-M7draft status | 2 | <12 | 37.4e |
acetohydroxamic acidf | n.a. | 72 | <73 | 2.5g |
EDTAh | ICH-M7 | 12 | <6 | 5h |
cysteamine·HCli | n.a. | 200 | <518 | 14.4j |
The bulk SF2a-TT15 is ≥100 times more concentrated than the formulated vaccine candidate.
N-Hydroxysuccinimide is a byproduct resulting from GMBS coupling to TT or from its hydrolysis into GMBA. Here, we assume 100% formation of byproduct.
2019 specification for DMSO is 6400 mM, which corresponds to 5000 ppm per vaccine dose.
[(volume DMSO mL/total volume mL) × 1000 = g/L]/Mw (DMSO) g/mol thus (6.33/106.33) × 1000/78.13.
(0.26 g/100 mL) × 1000 mL/Mw: 69.49 g/mol.
Acetohydroxamic acid is used as a treatment for bladder infections. A normal dose is 12 mg/kg/day, which translates to 720 mg/day for a 60 kg adult. When applying a minimum 1000-fold decline with respect to process performance and an additional 10-fold safety margin, a maximum amount of 1/10000 of the starting concentration of thiol 3 is acceptable.
6.47 mg/mL: same concentration as thiol 3.
The concentration of EDTA in conjugation buffer is 5 mM.
Cysteamine·HCl is administered as a treatment for nephropathic cystinosis. A daily dose of 2 g/day is accepted. When applying a minimum 1000-fold decline with respect to process performance and an additional 10-fold safety margin, a maximum amount of 1/10000 of initial concentration is acceptable or 200 μg/dose.
(180 mg/110 mL total) *1000 mL/Mw: 113.61 g/mol. ICH: International Council for Harmonisation of Technical Requirements for Pharmaceuticals for Human Use by their flow paths, LP screen and open channel, respectively. GMBA: 4-maleimidobutyric acid.