BBB	Blood–brain barrier
CNS	Central nervous system
CRISPR	Clustered regularly interspaced short palindromic repeat
DOTAP	1,2-dioleoyl-sn-glycero-3-trimethylammonium propane
DS	Dermatan sulphate
ERT	Enzyme replacement therapy
FLS	Fibroblast-like synoviocytes
GAGs	Glycosaminoglycans
GvHD	Graft versus host disease
HS	Heparan sulphate
HSCT	Hematopoietic stem cell transplantation
IDUA	Alpha-L-iduronidase
LSDs	Lysosomal storage disorders
MPS I	Mucopolysaccharidosis type I
PUFA	Omega-3 polyunsaturated fatty acids
Trp	Tryptophan