Table 1.
Donor template sequence for CRISPR-mediated correction of the Y347X mutation
| ssODN | Sequence (5′ → 3′) |
|---|---|
| NdeI-Pde6b ssODN | AACAATGCAAGCATTCATTCCTTCGACCTCTGTTCTTTTCCCACAGC ACACCCCCGGCTGATCACTGGGCCCTGGCCAGTGGCCTTCCAACAT ATGTAGCTGAGAGTGGCTTTGTGAGTGTCCCTCTCCAGGCCTTGGC CTCTACTGGCCAGTGCTATGATATGTGCTAGCCTGCTACCTCCTATT AGCACATCCTGCTA |