Table 1.
Baseline characteristics
| DMD sample (n = 61) | |
|---|---|
| Age, years | |
| Mean (SD) | 8.0 (2.4) |
| Median (IQR) | 8 (6, 9) |
| Min, max | 5, 16 |
| By group, n (%)* | |
| 5–7 years | 29 (48) |
| 8–11 years | 29 (48) |
| 12–16 years | 3 (5) |
| NSAA total score | |
| Mean (SD) | 21.0 (8.1) |
| Median (IQR) | 23 (15, 27) |
| Min, max | 4, 33 |
| 6MWD (m) | |
| Mean (SD) | 348 (92) |
| Median (IQR) | 354 (311, 400) |
| Min, max | 108, 566 |
| Timed 10MWR test (s)† | |
| Mean (SD) | 7.5 (3.6) |
| Median (IQR) | 6.1 (5.2, 8.5) |
| Min, max | 3.4, 20.0 |
| Timed RFF (s)† | |
| Mean (SD) | 13.4 (15.9) |
| Median (IQR) | 6.8 (4.2, 12.0) |
| Min, max | 0.5, 63.0 |
| RFF | |
| Unable to RFF independently, n (%) | 19 (31) |
| Unable to RFF, even with use of a chair, n (%) | 6 (10) |
6MWD = six-minute walk distance; NSAA = North Star Ambulatory Assessment; RFF = rising from floor; SD = standard deviation
*While age categories 8-11y and 12-16y were initially investigated, the three patients in the 12-16y category were considered along with the 8-11y old boys, due to small sample size
†n = 55