| BCL11A | BAF Chromatin Remodeling Complex Subunit BCL11A |
| BDDs | blood disease disorders |
| BMT | bone marrow transplantation |
| Cas | CRISPR-associated protein |
| CRISPR | clustered regularly interspaced short palindromic repeat |
| crRNA | sequence-specific CRISPR RNA |
| EPO | erythropoietin |
| FOG | Friend of GATA |
| FOP | Friend of Prmt1 |
| GATA-1 | GATA-binding factor 1 |
| GATA-2 | GATA-binding factor 2 |
| GVHD | graft versus host disease |
| GETs | gene editing tools |
| HbF | hemoglobin F |
| HDR | homology-directed repair |
| HLA | human leukocyte antigen |
| HPFH | hereditary persistence of fetal hemoglobin |
| HSCs | hematopoietic stem cells |
| IDLVs | integrase-defective lentiviruses |
| iPSCs | in pluripotent stem cells |
| KLF1 | Kruppel Like Factor 1 |
| NF-E2 | Nuclear Factor, Erythroid 2 |
| NHEJ | non-homologous end joining |
| rAAV6 | recombinant adeno-associated viral vectors serotype 6 |
| RBCs | red blood cells |
| SCD | sickle cell disease |
| SCL | Stem Cell Leukemia |
| SOX6 | SRY-Box Transcription Factor 6 |
| ssODN | single-stranded oligodeoxynucleotide |
| TALENs | transcription activator-like effector nucleases |
| tracrRNA | trans-activating crRNA |
| ZBTB7A | Zinc Finger and BTB Domain Containing 7A |
| ZFNs | zinc-finger nucleases |