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. 2022 Jul 8;17:258. doi: 10.1186/s13023-022-02397-4

Table 1.

Terms for literature search

Concept 1 Concept 2
Health technology assessment OR Drugs for rare diseases OR
Reimbursement decision-making OR Orphan drugs OR
Coverage with evidence development OR Expensive drugs
Access with evidence development OR
Conditional coverage OR
Performance-based risk sharing arrangements OR
Managed entry agreements OR
Managed access programs