Table 2.

Ongoing interventional clinical trials for novel treatments in galactosemias.

Condition	Drug	Approach	Participant Age	Study Phase	Study Identifier
CG	AT-007	Enzyme inhibitor	2–18	2/3	NCT04902781
CG	AT-007	Enzyme inhibitor	18–55	1/2	NCT04117711
CG	BBC	Behavioral	0.2–4.5	N.A.	NCT03838016
CG	N.A.	Cryopreservation	4–12	N.A.	NCT04948658

Data retrieved from Clinicaltrials.gov, last accessed on 23 May 2022. BBC: babble boot camp; CG: classic galactosemia; N.A.: not applicable.