TABLE 3.
Condition a | HHS recommendation to RUSP | Status | Years |
---|---|---|---|
SCID | 2010 | 100% (53/53) | 10 |
CCHD | 2011 | 100% (53/53) | 9 |
Pompe | 2015 | 43% (23/53) | 5+ |
MPS I | 2016 | 39% (21/53) | 4+ |
X-ALD | 2016 | 34% (18/53) | 4+ |
SMA | 2018 | 43% (23/53) | 2+ |
SCID, Severe Combined Immunodeficiency; CCHD, Critical Congenital Heart Disease; MPS I, Mucopolysaccharidosis Type I; X-ALD, X-Linked Adrenoleukodystrophy; SMA, Spinal Muscular Atrophy.