Number of patients screened | 33 |
Number of patients enrolled | 24 |
Number of patients evaluable for toxicity | 24 |
Number of patients evaluated for efficacy | 24 |
Evaluation method | RECIST 1.1 |
Response assessment, CR | 0(0%) |
Response assessment, PR | 20.8% |
Response assessment, SD | 2(8.3%) |
Response assessment, PD | 14(58.3%) |
Response assessment, Other | 3(16.7%) |
(Median) Duration assessments, PFS | 2.1 months; CI 2.1-4.3 |
(Median) Duration assessments, OS | 12.7 months; CI 5.8-NA |
(Median) Duration assessments, Response duration | 2.8 months |
Duration of treatment |
Three patients were not assessed (PD [n = 2) and death [n = 1)]. Phase Ia enrolled 2 patients with NET evaluated as one SD and one PD, and one NEC evaluated as PR.