| AAV | Adeno-associated virus |
| AMD | Age-related macular degeneration |
| AE | Adverse effect |
| BDNF | Brain-derived neurotrophic factor |
| BIV | Bovine immunodeficiency virus |
| BCVA | Best-corrected visual acuity |
| C3 | Exoenzyme C3 transferase |
| CA | Capsid |
| cDNA | Complementary DNA |
| CMV | Cytomegalovirus |
| CNTF | Ciliary neurotrophic factor |
| CNV | Choroidal neovascularization |
| cPPT | Central polypurine tract |
| Cas9 | CRISPR-associated protein 9 |
| CRISPR | Clustered regularly interspaced short palindromic repeats |
| DNA | Deoxyribonucleic acid |
| EIAV | Equine infectious anemia virus |
| ERG | Electroretinography |
| FAF | Fundus autofluorescence |
| FIV | Feline immunodeficiency virus |
| FGF | Fibroblast growth factor |
| GFP | Green fluorescent protein |
| GMP | Good manufacturing process |
| HIV-1 | Human immunodeficient virus 1 |
| hPEDF | Human pigment epithelium-derived factor |
| IDLV | Integrase-deficient lentiviral vector |
| IN | Integrase |
| IOP | Intraocular pressure |
| iPSC | Induced pluripotent stem cell |
| IRD | Inherited retinal dystrophies |
| IVNV | Intravitreal neovascularization |
| LTR | Long terminal repeat |
| LV | Lentiviral vector |
| MA | Matrix |
| miRNA | microRNA |
| mRNA | Messenger RNA |
| MV | Measles virus |
| NC | Nucleocapsid |
| NHP | Non-human primate |
| OCT | Optical coherence tomography |
| OIR | Oxygen-induced retinopathy |
| OLM | Outer limiting layer |
| ONL | Outer nuclear layer |
| PCR | Polymerase chain reaction |
| p.i. | Post injection |
| PRO | Protease |
| qPCR | Quantitative PCR |
| qRT-PCR | Quantitative RT-PCR |
| rAAV | Recombinant AAV |
| RCL | Recombinant-competent lentivirus |
| RGC | Retinal ganglion cell |
| RPE | Retinal pigment epithelium |
| RNA | Ribonucleic acid |
| ROP | Retinopathy of prematurity |
| RRE | Rev response element |
| RT | Reverse transcriptase |
| RRV | Ross River virus |
| SA | Splicing acceptor |
| scFV | Single-chain antibody |
| shRNA | Short hairpin RNA |
| SIN | Self-inactivating |
| SD | Splicing donor |
| seV | Sendai virus |
| sgRNA | Single guide RNA |
| SIV | Simian immunodeficiency virus |
| SFFV | Spleen focus-forming virus |
| sFlt-1 | Fms-like tyrosine kinase-1 |
| ssRNA | Single-strand RNA |
| SU | Surface |
| TAR | Tat activating region |
| TFF | Tangential flow filtration |
| TM | Transmembrane |
| TU | Transducing unit |
| VEGF | Vascular endothelial growth factor |
| VMD2 | Vitelliform macular dystrophy 2 |
| VSV-G | Vesicular stomatitis virus G |
| WPRE | Woodchuck hepatitis virus post-transcriptional regulatory element |
| WT | Wild type |
| Ψ | Packaging signal sequence |