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. 2022 Jul 31;14(8):1605. doi: 10.3390/pharmaceutics14081605
AAV Adeno-associated virus
AMD Age-related macular degeneration
AE Adverse effect
BDNF Brain-derived neurotrophic factor
BIV Bovine immunodeficiency virus
BCVA Best-corrected visual acuity
C3 Exoenzyme C3 transferase
CA Capsid
cDNA Complementary DNA
CMV Cytomegalovirus
CNTF Ciliary neurotrophic factor
CNV Choroidal neovascularization
cPPT Central polypurine tract
Cas9 CRISPR-associated protein 9
CRISPR Clustered regularly interspaced short palindromic repeats
DNA Deoxyribonucleic acid
EIAV Equine infectious anemia virus
ERG Electroretinography
FAF Fundus autofluorescence
FIV Feline immunodeficiency virus
FGF Fibroblast growth factor
GFP Green fluorescent protein
GMP Good manufacturing process
HIV-1 Human immunodeficient virus 1
hPEDF Human pigment epithelium-derived factor
IDLV Integrase-deficient lentiviral vector
IN Integrase
IOP Intraocular pressure
iPSC Induced pluripotent stem cell
IRD Inherited retinal dystrophies
IVNV Intravitreal neovascularization
LTR Long terminal repeat
LV Lentiviral vector
MA Matrix
miRNA microRNA
mRNA Messenger RNA
MV Measles virus
NC Nucleocapsid
NHP Non-human primate
OCT Optical coherence tomography
OIR Oxygen-induced retinopathy
OLM Outer limiting layer
ONL Outer nuclear layer
PCR Polymerase chain reaction
p.i. Post injection
PRO Protease
qPCR Quantitative PCR
qRT-PCR Quantitative RT-PCR
rAAV Recombinant AAV
RCL Recombinant-competent lentivirus
RGC Retinal ganglion cell
RPE Retinal pigment epithelium
RNA Ribonucleic acid
ROP Retinopathy of prematurity
RRE Rev response element
RT Reverse transcriptase
RRV Ross River virus
SA Splicing acceptor
scFV Single-chain antibody
shRNA Short hairpin RNA
SIN Self-inactivating
SD Splicing donor
seV Sendai virus
sgRNA Single guide RNA
SIV Simian immunodeficiency virus
SFFV Spleen focus-forming virus
sFlt-1 Fms-like tyrosine kinase-1
ssRNA Single-strand RNA
SU Surface
TAR Tat activating region
TFF Tangential flow filtration
TM Transmembrane
TU Transducing unit
VEGF Vascular endothelial growth factor
VMD2 Vitelliform macular dystrophy 2
VSV-G Vesicular stomatitis virus G
WPRE Woodchuck hepatitis virus post-transcriptional regulatory element
WT Wild type
Ψ Packaging signal sequence