| AAT | alpha-1 antitrypsin |
| ABCA4 | ATP-binding cassette subfamily A member 4 |
| AAV | adeno-associated virus |
| CRISPR | clustered regularly interspersed short palindromic repeats |
| DsRed | red fluorescent protein derived from Discosoma coral |
| EGFP | enhanced green fluorescent protein |
| ERG | electroretinogram |
| GFP | green fluorescent protein |
| IRBP | interphotoreceptor retinoid-binding protein |
| MOP | mouse opsin promoter |
| NF-κB | nuclear factor kappa B |
| Nrl | neural retina leucine zipper |
| Pde6b | phosphodiesterase 6B |
| PEI | polyethylenimine |
| rd1 | retinal degeneration 1 |
| rds | retinal degeneration slow |
| Rho | rhodopsin |
| RPE | retinal pigment epithelium |
| RPE65 | retinal pigment epithelium-specific protein 65 |
| S/MAR | scaffold matrix attachment region |
| TNFα | tumour necrosis factor alpha |
| VMD2 | vitelliform macular dystrophy 2 |
| WPRE | Woodchuck hepatitis virus post-transcriptional regulatory element |