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. 2022 Nov 2;57(Suppl 1):100–416. doi: 10.1038/s41409-022-01798-0
Feature MHC Class II Deficiency (n = 8)
Median (range) or N
CGD (n = 8)
Median(range) or N
Age (years) 1.71 (0.5-5.1) 7.14 (5.1-11)
Gender (F/M) 4/4 2/6
MRD/MUD 7/1 7/1
Cumulative Busulfan level (mg/L.h) 57 (50-70) 52.7 (46-62)
Time to Neutrophil engraftment (days) 24(16-30) 20 (17-26)
Time to Platelet engraftment (days) 33(25-65) 18(17-47)
Infused nucleated cell dose (X 108/kg) 5.7 (4-14) 4.2 (1.1-7.5)
Infused CD34 cell dose (X 106/kg) 12 (2.51-21.9) 7.6 (3.3-10.7)
Acute GVHD Grade II-IV 1 (grade II) 1 (grade II)