| 14BT057 (18) | SOC (10) | |
|---|---|---|
| Age at transplant (years), median (range) | 10.6 (0.3-20.0) | 8 (1.7-11.7) |
| Female, # (%) | 6 (33) | 5 (50) |
| Race/Ethnicity, n (%) | ||
| White, Non-Hispanic | 13 (72) | 6 (60) |
| African-American | - | 1 (10) |
| Hispanic | 5 (28) | 1 (10) |
| Middle Eastern | - | 2 (20) |
| Disease, n (%) | ||
| Severe Aplastic Anemia (SAA) | ||
| Idiopathic | 9 (50) | 3 (30) |
| SAA with >10% PNH | 1 (6) | - |
| Hepatitis associated | 2 (11) | 4 (40) |
| Diamond-Blackfan Anemia | 1 (6) | 1 (10) |
| Severe Congenital Neutropenia | 4 (22) | 1 (10) |
| Congenital Sideroblastic Anemia | - | 1 (10) |
| Amegakaryocytic Thrombocytopenia | 1 (6) | - |
| Time from diagnosis to SCT (years), median (range) | 0.2 (0.1 to 15) | 0.2 (0.1 to 9.1) |
| More than 10 lifetime PRBC transfusions pre-SCT | 1 (6) | 2 (20) |
| Prior treatments n (%) | 1 (6) | - |
| IST for aplastic anemia (hATG/CSA) Steroids for hepatitis/DBA | 2 (11) | 4 (40) |
| Chronic RBC/platelet Transfusions | 2 (11) | 1 (10) |
| Chronic G-CSF | 4 (22) | 1 (10) |
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