Wild-type mice (CD-1) were administered a single i.v. bolus of 0.5 mg/kg hMUT mRNA encapsulated in a biodegradable LNP and sacrificed at various time points (2, 6, 16 hr, 1, 2, 3, 5, 7 days; n = 3 mice/time point).
(A) Ionizable lipid in liver extracts was quantified by LC-MS/MS.
(B) Hepatic hMUT mRNA following hMUT administration was quantified using a branched-chain DNA (bDNA) assay.
(C) hMUT mRNA distribution was determined by in situ hybridization (ISH) using an hMUT mRNA-specific probe.
(D) Hepatic hMUT protein levels following hMUT mRNA administration. hMUT protein was quantified by LC-MS/MS.
****p < 0.0001, p values obtained from Tukey’s multiple-comparison test after one-way ANOVA.