Table 2.
Tumor responses and disease control.
| Patient | Change of PS | Best systemic response | Best radiographic LM response | Neurological symptomatic response | PFS (months) | adverse events |
|---|---|---|---|---|---|---|
| 1 | 4→2 | PR | Disappeared | Improved | Stable (22 FU) | Hypertension and prolonged APTT |
| 2 | 4→1 | PR | Improved | Improved | 11 (died) | Rash |
| 3 | 3→0 | NA | Improved | Disappeared | 10 (alive) | |
| 4 | 4→2 | PR | Improved | Improved | Stable (15 FU) | Elevated CPK and transaminase |
| 5 | 2→0 | NA | Disappeared | Disappeared | Stable (18 FU) | Diarrhea |
NA, not available; SD, stable disease; PR, partial response; CR, complete response; FU, follow-up.