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. 2022 Nov 23;13:1065163. doi: 10.3389/fneur.2022.1065163

Table 1.

Summary of pedunculopontine nucleus involvement in dystonia-related autopsy reports.

Report Diagnosis Age at onset/death, yr Family history Gender Genotype Phenotype PPN pathology Other neuropathology
Isolated dystonia
Zweig et al. (10) DMD 14/29 Likely M - Dystonic posturing of right foot and both hands, mild head forward, hypomimia Occasional NFTs Neural loss in LC; NFTs in LC, SNpc and DRN
Meige syndrome 33/68 - M - Oromandibular dystonia, occasional blepharospasm, Retrocollis Neural loss Neural loss in SNpc, DRN and LC and CSRN; astrocytic proliferation and extracellular neuromelanin pigment in SN and LC; infrequent NFTs in SN
McNaught et al. (8) DMD 5/83 Yes F DYT1-GAG deletion No details Perinuclear ubiquitin and torsinA-positive inclusions in cholinergic neurons Ubiquitin and torsinA-positive inclusions in RF, PAG, SC, CN and griseum centrale mesencephali; Tau and ubiquitin-positive inclusions in SNpc and LC
Focal non-progressive dystonia 19/86 Yes M DYT1-GAG deletion
DMD 10/78 Yes M DYT1-GAG deletion
Generalized dystonia 8/33 Likely M DYT1-GAG deletion
Mente et al. (9) CD 47/52 - F - Left torticollis Cholinergic neural loss None
CD 40/65 - F - Right laterocollis
CD Unknown/70 - M - No details
CD 53/75 F - No details
CD Unknown/78 - F - No details
CD Unknown/81 - F - Dystonic head tremor
CD 41/84 - F - Left laterocollis
CD Unknown/85 - F - Dystonic head tremor
Combined dystonia -
Sasaki et al. (57) Early onset Parkinson's disease 33/70 - F Parkin-homozygous exon 3 deletion Juvenile parkinsonism, choreic dyskinesia of limb and trunk, gait disturbance, bilateral extension of big toes Basophilic, α-synuclein and ubiquitin-positive inclusions Melanin-containing neurons loss in SNpc and LC; extraneuronal melanin pigments in LC

CD, cervical dystonia; CN, cuneiform nucleus; CSRN, central superior raphe nucleus; DMD, dystonia musculorum deformans; DRN, dorsal raphe nucleus; LC, locus ceruleus; NFTs, neurofibrillary tangles; PAG, periaqueductal gray; PPN, pedunculopontine nucleus; RF, reticular formation; SC, superior colliculus; SNpc, substantia nigra pars compacta.