AAVs	Adeno-associated viruses
ABEs	Adenosine base editors
ADAR2	Adenosine deaminase domain of adenosine deaminase acting on the RNA-2
Ads	Adenoviral vectors
CRISPR-Cas9	Clustered Regularly Interspaced Short Palindromic Repeats CRISPR-Cas9 nuclease
CBEs	Cytosine base editors
CTL	Cytotoxic T lymphocyte
dCas9	Dead Cas9
DDR	DNA damage response
DSBs	Double-strand breaks
FA	Fanconi anemia
HbF	Fetal hemoglobin
HDAd	Helper-dependent adenovirus
HSC	Hematopoietic stem cell
HSPCs	Hematopoietic stem and progenitor cells
HPFH	Hereditary persistence of fetal hemoglobin
HDR	Homologous directed repair
HIV	Human immunodeficiency virus
IAV	Influenza A virus
ITRs	Inverted terminal repeats
LbL	Layer-by-layer
LVs	Lentiviral vectors lvs
LCMV	Lymphocytic choriomeningitis virus
MHC	Major histocompatibility complex
MMEJ	Microhomology-mediated end joining
Nab	Neutralizing antibodies
NHEJ	Non-homologous end joining
PNAs	Peptide nucleic acids
PLGA	Poly-lactic-co-glycolic acid
pegRNA	Prime editing guide RNA
PE	Prime editors
PAM	Protospacer adjacent motif
SARS-CoV-2	Severe acute respiratory syndrome coronavirus 2
ssODN	Single-stranded oligodeoxynucleotide
TALENs	Transcription activator-like effector nucleases
VOCs	Vaso-occlusive crises
VSV	Vesicular stomatitis virus
VSV-G	Vesicular stomatitis virus glycoprotein
WAS	Wiskott-Aldrich syndrome
XLMTM	X-linked myotubular myopathy and Duchenne’s muscular dystrophy
X-SCID	X-linked Severe Combined Immunodeficiency
ZFNs	Zinc-finger nucleases