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. 2022 Dec 8;23(24):15525. doi: 10.3390/ijms232415525
SID serum-induced differentiation
iPSCs induced pluripotent stem cells
CMD congenital muscular dystrophy
EDMD2 Emery–Dreifuss muscular dystrophy 2
EDMD3 Emery–Dreifuss muscular dystrophy 3
MTR missense tolerance ratio
CBE cytosine base editor
PAM protospacer-adjacent motif