SID | serum-induced differentiation |
iPSCs | induced pluripotent stem cells |
CMD | congenital muscular dystrophy |
EDMD2 | Emery–Dreifuss muscular dystrophy 2 |
EDMD3 | Emery–Dreifuss muscular dystrophy 3 |
MTR | missense tolerance ratio |
CBE | cytosine base editor |
PAM | protospacer-adjacent motif |