Table 4.
Response at 6 months in SAA vs. VSAA.
| Group A Pediatric patients with IST + EPAG |
Group B Pediatric patients with IST only |
P | |
|---|---|---|---|
| SAA | n = 6 | n = 18 | |
| Response n (%) OR CR |
5 (83.3) 4 (66.7) |
12 (66.7) 2 (11.1) |
0.629 0.018 |
| VSAA | n = 9 | n = 27 | |
| Response n (%) OR CR |
5 (55.6) 3 (33.3) |
14 (51.9) 4 (14.8) |
1.000 0.333 |
Note: EPAG, eltrombopag; IST, immunosuppressive therapy; CR, complete response; OR, overall response; SAA, severe aplastic anemia; VSAA, very severe aplastic anemia.