Table 1.
Baseline characteristics of all patients
| Pediatric walker | Adult walker | |
| (n = 114) | (n = 117) | |
| Age at symptom onset (months) | 40.8 [30.4;51.5] | 138.6 [113.6;163.7] |
| Age at start of treatment (months) | 103.3 [89;117.6] | 443.5 [405.1;481.9] |
| SMN2 copy number | ||
| 1 SMN2 | 0 (0%) | 2 (1.7%) |
| 2 SMN2 | 10 (8.8%) | 4 (3.4%) |
| 3 SMN2 | 35 (30.7%) | 24 (20.5%) |
| ≥4 SMN2 | 57 (50%) | 67 (57.3%) |
| unknown | 12 (10.5%) | 20 (17.1%) |
| FVC% (n) | 89.6 [85.4;93.8] (29) | 93.0 [89.6;96.4] (85) |
| HMFSE score (n) | 51.1 [48.6;53.7] (88) | 46.2 [43.2;49.5] (105) |
| RULM score (n) | 32.4 [30.8;34.2] (70) | 34.7 [33.7;35.9] (101) |
| 6MWT (n) | 329.2 [264.9;393.6] (50) | 353.8 [312.5;403.7] (84) |
| Fatigue | 27 (23.7%) | 42 (35.9%) |
Baseline characteristics of all patients allocated to pediatric and adult walkers. Data are listed as mean and 99% confidence interval or n (%).