TABLE 2.

Working group 1 members

Expertise	Investigator	Affiliation
Co-Chairs	Margaret Ragni, MD, MPH	University of Pittsburgh
	Lindsey George, MD	University of Pennsylvania
Biostatistics	Alfonso Iorio, MD, PhD	McMaster University, CA
	John Scott, PhD	Food & Drug Administration/Center  Biologics Evaluation
Clinical Trials	James Casella, MD	Johns Hopkins University
	Charles Hay, MD	Manchester Royal Infirmary, UK
	Alice Long, PhD	Benaroya Research Institute
	Marilyn Manco-Johnson, MD	University of Colorado
Industry	Marcus Carr, MD, PhD	Spark Therapeutics
Haemophilia Community Perspective	Jorge de la Riva	National Haemophilia Foundation
	Ilene Goldberg, RN	Weill Cornell Medical College
	Matthew Igelman	PWH, Haemophilia Federation of America
	Jay Konduros	PWH, Gene Trial Participant

PWH, person with haemophilia.