| CC | corpus callosum |
| CSF | cerebrospinal fluid |
| DQ | developmental quotient |
| ERT | enzyme replacement therapy |
| GAGs | glycosaminoglycans |
| HSCT | hematopoietic stem cell transplantation |
| HSPC | hematopoietic stem and progenitor cell |
| IDUA | alpha-L-iduronidase |
| IHOMS | internal hypertrophy of the occipitomastoid suture |
| MPS 1 | Mucopolysaccharidosis type 1 |
| MRI | magnetic resonance imaging |
| MRS | magnetic resonance spectroscopy |
| PVS | perivascular spaces |
| WM | white matter |
| WMA | white matter abnormalities |
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