Table 3.
Association of ePRO scores with patient activity.
| Overall cohorts (A + B) |
Cohort A |
Cohort B |
||||||
|---|---|---|---|---|---|---|---|---|
| ePRO domain | Effect on activity (95% CI) | ePRO domain | Effect on activity (95% CI) | ePRO domain | Effect on activity (95% CI) | |||
| ↑ Patient activity | ↑ QLQ30 physical function | 52.6 (28.8–52.6) | ↑ Patient activity | ↑ QLQ30 physical function | 75.8 (29.0–122.6) | ↑ Patient activity | ↑ QLQ30 physical function | 37.4 (19.2–55.5) |
| ↑ Patient activity | ↑ QLQ30 global health | 20 (3.2–36.8) | ↑ Patient activity | ↑ QLQ30 global health | 42.3 (6.7–77.8) | ↑ Patient activity | ↑ QLQ30 global health | 10.5 (−2.8 to 23.8) |
| ↑ Patient activity | ↓ MY20 disease burden | −26.7 (−52.6 to −0.9) | ↑ Patient activity | ↓ MY20 disease burden | −47.2 (−97.3 to 3) | ↑ Patient activity | ↓ MY20 disease burden | 14 (−37.6 to 8.4) |
| Patient activity | MY20 future perspective | −20 (−43.4 to 3.4) | Patient activity | MY20 future perspective | −19.0 (−57.7 to 19.7) | Patient activity | MY20 future perspective | −21.5 (−44.1 to 1.1) |
| Patient activity | MY20 self-body image | −5.4 (−9 to 19) | Patient activity | MY20 self-body image | −6.5 (−1 to 17) | Patient activity | MY20 self-body image | −12.5 (−29 to 5) |
↑ Patient activity signifies increased step counts. ↑ QLQ30 physical function signifies improvement in physical function PRO scores. ↑ QLQ30 global health signifies improvement in global health PRO scores. ↓ MY20 disease burden signifies improvement in disease burden PRO scores.