Figure - PMC

Skip to main content

An official website of the United States government

Here's how you know

Here's how you know

Official websites use .gov
A .gov website belongs to an official government organization in the United States.

Secure .gov websites use HTTPS
A lock ( ) or https:// means you've safely connected to the .gov website. Share sensitive information only on official, secure websites.

View full-text article in PMC

. 2023 Aug 7;13(8):1227. doi: 10.3390/biom13081227

Search in PMC
Search in PubMed
View in NLM Catalog
Add to search

© 2023 by the authors.

Licensee MDPI, Basel, Switzerland. This article is an open access article distributed under the terms and conditions of the Creative Commons Attribution (CC BY) license (https://creativecommons.org/licenses/by/4.0/).

PMC Copyright notice

Literature evidence map for chaperones in lysosomal storage disorders. Orange circles = preclinical studies. Blue squares = clinical studies. Closed squares = one study; open square = 2 articles reporting data from the same study. ^a One citation reported an analysis including both chaperones N-butyl-deoxynojirimycin (NB-DNJ) and 1-deoxynojirimycin (DNJ), counted twice. Abbreviations: DGJ, 1-deoxygalactonojirimycin/migalastat; DNJ, 1-deoxynojirimycin; NB-DNJ, N-butyl-deoxynojirimycin/miglustat; NN-DNJ, N-Nonyldeoxynojirimycin; NOEV, N-octyl-4-epi-beta-valienamine; NPC, Niemann–Pick Disease Type C; MPSI, Muco-polysaccharidosis 1.