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Timelines of ALD, MLD and GLD: from recognition to the development of gene therapy. Development of gene therapy for the major primary leukodystrophies has taken well over a century to reach clinics. However, it is expected that the development and approval of gene therapy for similar diseases may be much faster since most of the footwork has been carried out and many of the pitfalls have been revealed and tackled in subsequent studies. AR: autosomal recessive; GT: gene therapy.
