Martina Fiumara
Martina Fiumara
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
2Vita-Salute San Raffaele University, Milan, Italy
1,2,#,
Samuele Ferrari
Samuele Ferrari
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
2Vita-Salute San Raffaele University, Milan, Italy
1,2,✉,#,
Attya Omer-Javed
Attya Omer-Javed
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Stefano Beretta
Stefano Beretta
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Luisa Albano
Luisa Albano
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Daniele Canarutto
Daniele Canarutto
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
2Vita-Salute San Raffaele University, Milan, Italy
3Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,2,3,
Angelica Varesi
Angelica Varesi
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Chiara Gaddoni
Chiara Gaddoni
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Chiara Brombin
Chiara Brombin
4University Center for Statistics in the Biomedical Sciences, Vita-Salute San Raffaele University, Milan, Italy
4,
Federica Cugnata
Federica Cugnata
4University Center for Statistics in the Biomedical Sciences, Vita-Salute San Raffaele University, Milan, Italy
4,
Erika Zonari
Erika Zonari
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Matteo Maria Naldini
Matteo Maria Naldini
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Matteo Barcella
Matteo Barcella
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Bernhard Gentner
Bernhard Gentner
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
1,
Ivan Merelli
Ivan Merelli
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
5National Research Council, Institute for Biomedical Technologies, Segrate, Italy
1,5,
Luigi Naldini
Luigi Naldini
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
2Vita-Salute San Raffaele University, Milan, Italy
1,2,✉
1San Raffaele Telethon Institute for Gene Therapy, IRCCS San Raffaele Scientific Institute, Milan, Italy
2Vita-Salute San Raffaele University, Milan, Italy
3Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy
4University Center for Statistics in the Biomedical Sciences, Vita-Salute San Raffaele University, Milan, Italy
5National Research Council, Institute for Biomedical Technologies, Segrate, Italy
Subject terms: Targeted gene repair, Stem-cell biotechnology, Haematopoietic stem cells
© The Author(s) 2024
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