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[Preprint]. 2024 Sep 22:2024.09.18.613594. [Version 1] doi: 10.1101/2024.09.18.613594

Peptide-MHC-targeted retroviruses enable in vivo expansion and gene delivery to tumor-specific T cells

Ellen JK Xu, Blake E Smith, Winiffer D Conce Alberto, Michael J Walsh, Birkley Lim, Megan T Hoffman, Li Qiang, Jiayi Dong, Andrea Garmilla, Qingyang Henry Zhao, Caleb R Perez, Stephanie A Gaglione, Connor S Dobson, Michael Dougan, Stephanie K Dougan, Michael E Birnbaum
PMCID: PMC11429759  PMID: 39345591

Abstract

Tumor-infiltrating-lymphocyte (TIL) therapy has demonstrated that endogenous T cells can be harnessed to initiate an effective anti-tumor response. Despite clinical promise, current TIL production protocols involve weeks-long ex vivo expansions which can affect treatment efficacy. Therefore, additional tools are needed to engineer endogenous tumor-specific T cells to have increased potency while mitigating challenges of manufacturing. Here, we present a strategy for pseudotyping retroviral vectors with peptide-major histocompatibility complexes (pMHC) for antigen-specific gene delivery to CD8 T cells and examine the efficacy of these transduced cells in immunocompetent mouse models. We demonstrate that pMHC-targeted viruses are able to specifically deliver function-enhancing cargoes while simultaneously activating and expanding anti-tumor T cells. The specificity of these viral vectors enables in vivo engineering of tumor-specific T cells, circumventing ex vivo manufacturing processes and improving overall survival in B16F10-bearing mice. Altogether, we have established that pMHC-targeted viruses are efficient vectors for reprogramming and expanding tumor-specific populations of T cells directly in vivo , with the potential to substantially streamline engineered cell therapy production for a variety of applications.

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