1American Family Children’s Hospital, University of Wisconsin School of Medicine and Public Health, Madison, WI USA
2Department of Pediatric Neurology, Hospital Universitari Vall d’Hebron, Barcelona, Spain
3Department of Physical Medicine and Rehabilitation, Hôpital Femme Mère Enfant - Hospices Civils de Lyon, Lyon, France
4Department of Pediatrics and Child Health, Kurume University School of Medicine, Kurume, Japan
5Institute of Medical Genetics, Tokyo Women’s Medical University, Tokyo, Japan
6Department of Paediatric Neurology, Reference Centre for Neuromuscular Disorders AOC, and Paediatric Clinical Research Unit Children’s Hospital, Toulouse University Hospital Center, Toulouse, France
7Department of Paediatric Neurology, Neuromuscular Reference Centre for Children, University Hospitals Leuven, Leuven, Belgium
8Department of Development and Regeneration, KU Leuven, Leuven, Belgium
9Department of Neurology, The Royal Children’s Hospital, Melbourne, Victoria Australia
10The Murdoch Children’s Research Institute, Parkville, Victoria Australia
11Paediatric Neurology, Catholic University, Rome, Italy
12Nemo Clinical Centre, Fondazione Policlinico Gemelli, IRCCS, Rome, Italy
13Children’s Hospital of The King’s Daughters, Norfolk, VA USA
14Department of Neurology, Boston Children’s Hospital, Harvard Medical School, Boston, MA USA
15Departments of Neurology and Neurosurgery and Pediatric, McGill University, Montreal, Quebec Canada
16Centre for Outcomes Research and Evaluation, Research Institute of the McGill University Health Centre, Montreal, Quebec Canada
17Novartis Pharmaceuticals, East Hanover, NJ USA
18Novartis Pharmaceuticals, London, UK
19Novartis Pharmaceuticals, Basel, Switzerland
20UMC Utrecht Brain Center, Department of Neurology and Neurosurgery, University Medical Center Utrecht, Utrecht, The Netherlands