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Molecular Therapy. Methods & Clinical Development logoLink to Molecular Therapy. Methods & Clinical Development
. 2019 May 1;13:431. doi: 10.1016/j.omtm.2019.04.005

Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction

Sang-oh Han, Giuseppe Ronzitti, Benjamin Arnson, Christian Leborgne, Songtao Li, Federico Mingozzi, Dwight Koeberl
PMCID: PMC6500922  PMID: 31073535

(Molecular Therapy - Methods & Clinical Development 4, 126–136; March 17, 2017)

An incorrect version of Figure 1E appeared in the published article due to an error in the calculation of plasma GAA. The correct figure appears below.

Figure 1E.

Figure 1E

Comparison of Liver Depot Gene Therapy with ERT (Corrected)


Articles from Molecular Therapy. Methods & Clinical Development are provided here courtesy of American Society of Gene & Cell Therapy

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