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[Preprint]. 2023 Feb 8:2023.02.06.23285528. [Version 1] doi: 10.1101/2023.02.06.23285528

Trials underestimate the impact of preventive treatment for household contacts exposed to multidrug-resistant tuberculosis: a simulation study

Parastu Kasaie, Jeff Pennington, Amita Gupta, David W Dowdy, Emily A Kendall
PMCID: PMC9934809  PMID: 36798407

Abstract

Background

Several clinical trials of tuberculosis preventive treatment (TPT) for household contacts of patients with multidrug-resistant tuberculosis (MDR-TB) are nearing completion. The potential benefits of TPT for MDR-TB contacts extend beyond the outcomes that clinical trials can measure.

Methods

We developed an agent-based, household-structured TB and MDR-TB transmission model, calibrated to an illustrative setting in India, the country accounting for 26% of global MDR-TB burden. We simulated household contact investigation for contacts of patients with MDR-TB, comparing an MDR-TPT regimen against alternatives of isoniazid preventive treatment, household contact investigation without TPT, or no household contact intervention. We simulated outcomes of a clinical trial and estimated the patient-level and population-level effects over a longer time horizon.

Findings

During two years of follow-up per recipient, a simulated 6-month MDR-TPT regimen with 70% efficacy against both DS- and MDR-TB infection could prevent 72% [Interquartile range (IQR): 45 – 100%] of incident MDR-TB among TPT recipients (number needed to treat (NNT) 73 [44 – 176] to prevent one MDR-TB case), compared to household contact investigation without TPT. This NNT decreased to 54 [30 – 183] when median follow-up was increased from two to 16 years, to 27 [11 – Inf] when downstream transmission effects were also considered, and to 12 [8 – 22] when these effects were compared to a scenario of no household contact intervention.

Interpretation

If forthcoming trial results demonstrate efficacy, the long-term population impact of MDR-TPT implementation could be much greater than suggested by trial outcomes alone.

Funding

NIH K01AI138853 and K08AI127908; Johns Hopkins Catalyst Award.

Full Text Availability

The license terms selected by the author(s) for this preprint version do not permit archiving in PMC. The full text is available from the preprint server.


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